PKU Study: New Medication

KateGilmore

Hi everyone,

Last week, I just learned from my PKU-friend from the US, that there is a study / trial ongoing with a medication which helps PKUs absorbing the phe over urine.

If you are interested, you can find more information about it here:

https://pubmed.ncbi.nlm.nih.gov/30046012/

I find it very promissing and I'm excited about the first results with PKU patients!

🤗

Gregor Hammerschmidt

#1 KateGilmore thanks for sharing. It's a paper from 2018. I think its in connection to BH4.

KateGilmore

BH4 is Kuvan, right? Then it is not the same. My friend is on Kuvan currently but will stop it because she wants to take part in the study for this new product then. As soon as I have more information, I will share it. 😊

Gregor Hammerschmidt

#3 KateGilmore From briefly reading it - it might be PEG-PAL being talked about scientifically. I will ask someone to verify this.